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For: Wang D, Tai PWL, Gao G. Adeno-associated virus vector as a platform for gene therapy delivery. Nat Rev Drug Discov. 2019;18:358-378. [PMID: 30710128 DOI: 10.1038/s41573-019-0012-9] [Cited by in Crossref: 332] [Cited by in F6Publishing: 276] [Article Influence: 166.0] [Reference Citation Analysis]
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1 Vigil TN, Zhang-Hulsey D, Santos JL, Patrick Hussmann G. Expediting in vitro characterization of mRNA-based gene therapies via high-content fluorescent imaging. Anal Biochem 2021;627:114259. [PMID: 34033800 DOI: 10.1016/j.ab.2021.114259] [Reference Citation Analysis]
2 De Giorgi M, Li A, Hurley A, Barzi M, Doerfler AM, Cherayil NA, Smith HE, Brown JD, Lin CY, Bissig KD, Bao G, Lagor WR. Targeting the Apoa1 locus for liver-directed gene therapy. Mol Ther Methods Clin Dev 2021;21:656-69. [PMID: 34141821 DOI: 10.1016/j.omtm.2021.04.011] [Reference Citation Analysis]
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4 Boon N, Alves CH, Mulder AA, Andriessen CA, Buck TM, Quinn PMJ, Vos RM, Koster AJ, Jost CR, Wijnholds J. Defining Phenotype, Tropism, and Retinal Gene Therapy Using Adeno-Associated Viral Vectors (AAVs) in New-Born Brown Norway Rats with a Spontaneous Mutation in Crb1. Int J Mol Sci 2021;22:3563. [PMID: 33808129 DOI: 10.3390/ijms22073563] [Reference Citation Analysis]
5 Tornabene P, Trapani I. Can Adeno-Associated Viral Vectors Deliver Effectively Large Genes? Human Gene Therapy 2020;31:47-56. [DOI: 10.1089/hum.2019.220] [Cited by in Crossref: 10] [Cited by in F6Publishing: 9] [Article Influence: 10.0] [Reference Citation Analysis]
6 Westhaus A, Cabanes-Creus M, Rybicki A, Baltazar G, Navarro RG, Zhu E, Drouyer M, Knight M, Albu RF, Ng BH, Kalajdzic P, Kwiatek M, Hsu K, Santilli G, Gold W, Kramer B, Gonzalez-Cordero A, Thrasher AJ, Alexander IE, Lisowski L. High-Throughput In Vitro, Ex Vivo, and In Vivo Screen of Adeno-Associated Virus Vectors Based on Physical and Functional Transduction. Hum Gene Ther 2020;31:575-89. [PMID: 32000541 DOI: 10.1089/hum.2019.264] [Cited by in Crossref: 17] [Cited by in F6Publishing: 14] [Article Influence: 17.0] [Reference Citation Analysis]
7 Zekonyte U, Bacman SR, Moraes CT. DNA-editing enzymes as potential treatments for heteroplasmic mtDNA diseases. J Intern Med 2020;287:685-97. [PMID: 32176378 DOI: 10.1111/joim.13055] [Cited by in Crossref: 6] [Cited by in F6Publishing: 5] [Article Influence: 6.0] [Reference Citation Analysis]
8 Bankoti K, Generotti C, Hwa T, Wang L, O'Malley BW Jr, Li D. Advances and challenges in adeno-associated viral inner-ear gene therapy for sensorineural hearing loss. Mol Ther Methods Clin Dev 2021;21:209-36. [PMID: 33850952 DOI: 10.1016/j.omtm.2021.03.005] [Reference Citation Analysis]
9 Stevens L, Larsen LE, Van Lysebettens W, Carrette E, Boon P, Raedt R, Vonck K. Optimized Parameters for Transducing the Locus Coeruleus Using Canine Adenovirus Type 2 (CAV2) Vector in Rats for Chemogenetic Modulation Research. Front Neurosci 2021;15:663337. [PMID: 33927593 DOI: 10.3389/fnins.2021.663337] [Reference Citation Analysis]
10 Chung SH, Mollhoff IN, Mishra A, Sin TN, Ngo T, Ciulla T, Sieving P, Thomasy SM, Yiu G. Host Immune Responses after Suprachoroidal Delivery of AAV8 in Nonhuman Primate Eyes. Hum Gene Ther 2021;32:682-93. [PMID: 33446041 DOI: 10.1089/hum.2020.281] [Cited by in Crossref: 5] [Cited by in F6Publishing: 4] [Article Influence: 5.0] [Reference Citation Analysis]
11 Johnson TB, White KA, Brudvig JJ, Cain JT, Langin L, Pratt MA, Booth CD, Timm DJ, Davis SS, Meyerink B, Likhite S, Meyer K, Weimer JM. AAV9 Gene Therapy Increases Lifespan and Treats Pathological and Behavioral Abnormalities in a Mouse Model of CLN8-Batten Disease. Mol Ther 2021;29:162-75. [PMID: 33010819 DOI: 10.1016/j.ymthe.2020.09.033] [Cited by in Crossref: 6] [Cited by in F6Publishing: 3] [Article Influence: 6.0] [Reference Citation Analysis]
12 He X, Urip BA, Zhang Z, Ngan CC, Feng B. Evolving AAV-delivered therapeutics towards ultimate cures. J Mol Med (Berl) 2021;99:593-617. [PMID: 33594520 DOI: 10.1007/s00109-020-02034-2] [Cited by in Crossref: 4] [Cited by in F6Publishing: 1] [Article Influence: 4.0] [Reference Citation Analysis]
13 Ogden PJ, Kelsic ED, Sinai S, Church GM. Comprehensive AAV capsid fitness landscape reveals a viral gene and enables machine-guided design. Science 2019;366:1139-43. [PMID: 31780559 DOI: 10.1126/science.aaw2900] [Cited by in Crossref: 82] [Cited by in F6Publishing: 53] [Article Influence: 82.0] [Reference Citation Analysis]
14 Chen W, Yao S, Wan J, Tian Y, Huang L, Wang S, Akter F, Wu Y, Yao Y, Zhang X. BBB-crossing adeno-associated virus vector: An excellent gene delivery tool for CNS disease treatment. J Control Release 2021;333:129-38. [PMID: 33775685 DOI: 10.1016/j.jconrel.2021.03.029] [Reference Citation Analysis]
15 Lee D, Liu J, Junn HJ, Lee EJ, Jeong KS, Seol DW. No more helper adenovirus: production of gutless adenovirus (GLAd) free of adenovirus and replication-competent adenovirus (RCA) contaminants. Exp Mol Med 2019;51:1-18. [PMID: 31659156 DOI: 10.1038/s12276-019-0334-z] [Cited by in Crossref: 1] [Cited by in F6Publishing: 2] [Article Influence: 0.5] [Reference Citation Analysis]
16 Hörner M, Jerez-Longres C, Hudek A, Hook S, Yousefi OS, Schamel WWA, Hörner C, Zurbriggen MD, Ye H, Wagner HJ, Weber W. Spatiotemporally confined red light-controlled gene delivery at single-cell resolution using adeno-associated viral vectors. Sci Adv 2021;7:eabf0797. [PMID: 34134986 DOI: 10.1126/sciadv.abf0797] [Reference Citation Analysis]
17 Dalwadi DA, Torrens L, Abril-Fornaguera J, Pinyol R, Willoughby C, Posey J, Llovet JM, Lanciault C, Russell DW, Grompe M, Naugler WE. Liver Injury Increases the Incidence of HCC following AAV Gene Therapy in Mice. Mol Ther 2021;29:680-90. [PMID: 33554867 DOI: 10.1016/j.ymthe.2020.10.018] [Cited by in Crossref: 4] [Cited by in F6Publishing: 2] [Article Influence: 4.0] [Reference Citation Analysis]
18 Wec AZ, Lin KS, Kwasnieski JC, Sinai S, Gerold J, Kelsic ED. Overcoming Immunological Challenges Limiting Capsid-Mediated Gene Therapy With Machine Learning. Front Immunol 2021;12:674021. [PMID: 33986759 DOI: 10.3389/fimmu.2021.674021] [Reference Citation Analysis]
19 Zhao H, Lee KJ, Daris M, Lin Y, Wolfe T, Sheng J, Plewa C, Wang S, Meisen WH. Creation of a High-Yield AAV Vector Production Platform in Suspension Cells Using a Design-of-Experiment Approach. Mol Ther Methods Clin Dev 2020;18:312-20. [PMID: 32671134 DOI: 10.1016/j.omtm.2020.06.004] [Cited by in Crossref: 4] [Cited by in F6Publishing: 4] [Article Influence: 4.0] [Reference Citation Analysis]
20 Liu Y, Tavana O, Gu W. p53 modifications: exquisite decorations of the powerful guardian. J Mol Cell Biol 2019;11:564-77. [PMID: 31282934 DOI: 10.1093/jmcb/mjz060] [Cited by in Crossref: 75] [Cited by in F6Publishing: 58] [Article Influence: 75.0] [Reference Citation Analysis]
21 Yoder KE, Rabe AJ, Fishel R, Larue RC. Strategies for Targeting Retroviral Integration for Safer Gene Therapy: Advances and Challenges. Front Mol Biosci 2021;8:662331. [PMID: 34055882 DOI: 10.3389/fmolb.2021.662331] [Reference Citation Analysis]
22 Gallego C, Gonçalves MAFV, Wijnholds J. Novel Therapeutic Approaches for the Treatment of Retinal Degenerative Diseases: Focus on CRISPR/Cas-Based Gene Editing. Front Neurosci 2020;14:838. [PMID: 32973430 DOI: 10.3389/fnins.2020.00838] [Cited by in Crossref: 3] [Cited by in F6Publishing: 1] [Article Influence: 3.0] [Reference Citation Analysis]
23 Valanti EK, Dalakoura-Karagkouni K, Siasos G, Kardassis D, Eliopoulos AG, Sanoudou D. Advances in biological therapies for dyslipidemias and atherosclerosis. Metabolism 2021;116:154461. [PMID: 33290761 DOI: 10.1016/j.metabol.2020.154461] [Cited by in Crossref: 4] [Cited by in F6Publishing: 3] [Article Influence: 4.0] [Reference Citation Analysis]
24 Luly KM, Choi J, Rui Y, Green JJ, Jackson EM. Safety considerations for nanoparticle gene delivery in pediatric brain tumors. Nanomedicine (Lond) 2020;15:1805-15. [PMID: 32698671 DOI: 10.2217/nnm-2020-0110] [Cited by in Crossref: 4] [Article Influence: 4.0] [Reference Citation Analysis]
25 Hu Y, Zhu Y, Sutherland ND, Wilson DR, Pang M, Liu E, Staub JR, Berlinicke CA, Zack DJ, Green JJ, Reddy SK, Mao HQ. Size-Controlled and Shelf-Stable DNA Particles for Production of Lentiviral Vectors. Nano Lett 2021;21:5697-705. [PMID: 34228937 DOI: 10.1021/acs.nanolett.1c01421] [Reference Citation Analysis]
26 Fakhiri J, Landegger LD, Grimm D. Breaking the sound barrier: Towards next-generation AAV vectors for gene therapy of hearing disorders. Hear Res 2020;:108092. [PMID: 33268240 DOI: 10.1016/j.heares.2020.108092] [Reference Citation Analysis]
27 Liu D, Zhu M, Zhang Y, Diao Y. Crossing the blood-brain barrier with AAV vectors. Metab Brain Dis 2021;36:45-52. [PMID: 33201426 DOI: 10.1007/s11011-020-00630-2] [Cited by in Crossref: 5] [Cited by in F6Publishing: 3] [Article Influence: 5.0] [Reference Citation Analysis]
28 Bennett A, Keravala A, Makal V, Kurian J, Belbellaa B, Aeran R, Tseng YS, Sousa D, Spear J, Gasmi M, Agbandje-McKenna M. Structure comparison of the chimeric AAV2.7m8 vector with parental AAV2. J Struct Biol 2020;209:107433. [PMID: 31859208 DOI: 10.1016/j.jsb.2019.107433] [Cited by in Crossref: 8] [Cited by in F6Publishing: 6] [Article Influence: 4.0] [Reference Citation Analysis]
29 Trapani I. Adeno-Associated Viral Vectors as a Tool for Large Gene Delivery to the Retina. Genes (Basel) 2019;10:E287. [PMID: 30970639 DOI: 10.3390/genes10040287] [Cited by in Crossref: 28] [Cited by in F6Publishing: 18] [Article Influence: 14.0] [Reference Citation Analysis]
30 Mietzsch M, Jose A, Chipman P, Bhattacharya N, Daneshparvar N, McKenna R, Agbandje-McKenna M. Completion of the AAV Structural Atlas: Serotype Capsid Structures Reveals Clade-Specific Features. Viruses 2021;13:101. [PMID: 33450892 DOI: 10.3390/v13010101] [Cited by in Crossref: 4] [Cited by in F6Publishing: 3] [Article Influence: 4.0] [Reference Citation Analysis]
31 Kruse RL, Huang Y, Shum T, Bai L, Ding H, Wang ZZ, Selaru FM, Kumbhari V. Endoscopic-mediated, biliary hydrodynamic injection mediating clinically relevant levels of gene delivery in pig liver. Gastrointest Endosc 2021:S0016-5107(21)01463-2. [PMID: 34197834 DOI: 10.1016/j.gie.2021.06.016] [Reference Citation Analysis]
32 Cui S, Ganjawala TH, Abrams GW, Pan ZH. Effect of Proteasome Inhibitors on the AAV-Mediated Transduction Efficiency in Retinal Bipolar Cells. Curr Gene Ther 2020;19:404-12. [PMID: 32072884 DOI: 10.2174/1566523220666200211111326] [Cited by in Crossref: 2] [Cited by in F6Publishing: 1] [Article Influence: 2.0] [Reference Citation Analysis]
33 Shotwell CR, Cleary JD, Berglund JA. The potential of engineered eukaryotic RNA-binding proteins as molecular tools and therapeutics. Wiley Interdiscip Rev RNA 2020;11:e1573. [PMID: 31680457 DOI: 10.1002/wrna.1573] [Cited by in Crossref: 3] [Cited by in F6Publishing: 3] [Article Influence: 1.5] [Reference Citation Analysis]
34 Junod SL, Saredy J, Yang W. Nuclear Import of Adeno-Associated Viruses Imaged by High-Speed Single-Molecule Microscopy. Viruses 2021;13:167. [PMID: 33499411 DOI: 10.3390/v13020167] [Cited by in Crossref: 2] [Cited by in F6Publishing: 1] [Article Influence: 2.0] [Reference Citation Analysis]
35 Prakoso D, Tate M, Blasio MJ, Ritchie RH. Adeno-associated viral (AAV) vector-mediated therapeutics for diabetic cardiomyopathy - current and future perspectives. Clin Sci (Lond) 2021;135:1369-87. [PMID: 34076247 DOI: 10.1042/CS20210052] [Reference Citation Analysis]
36 Tambuyzer E, Vandendriessche B, Austin CP, Brooks PJ, Larsson K, Miller Needleman KI, Valentine J, Davies K, Groft SC, Preti R, Oprea TI, Prunotto M. Therapies for rare diseases: therapeutic modalities, progress and challenges ahead. Nat Rev Drug Discov 2020;19:93-111. [PMID: 31836861 DOI: 10.1038/s41573-019-0049-9] [Cited by in Crossref: 46] [Cited by in F6Publishing: 32] [Article Influence: 23.0] [Reference Citation Analysis]
37 Hong L, Sun H, Amendt BA. MicroRNA function in craniofacial bone formation, regeneration and repair. Bone 2021;144:115789. [PMID: 33309989 DOI: 10.1016/j.bone.2020.115789] [Cited by in Crossref: 2] [Cited by in F6Publishing: 2] [Article Influence: 2.0] [Reference Citation Analysis]
38 Sam R, Ryan E, Daykin E, Sidransky E. Current and emerging pharmacotherapy for Gaucher disease in pediatric populations. Expert Opin Pharmacother 2021;22:1489-503. [PMID: 33711910 DOI: 10.1080/14656566.2021.1902989] [Cited by in Crossref: 1] [Article Influence: 1.0] [Reference Citation Analysis]
39 Markati T, Duis J, Servais L. Therapies in preclinical and clinical development for Angelman syndrome. Expert Opin Investig Drugs 2021;30:709-20. [PMID: 34112038 DOI: 10.1080/13543784.2021.1939674] [Cited by in Crossref: 1] [Article Influence: 1.0] [Reference Citation Analysis]
40 Li J, Zheng M, Shimoni O, Banks WA, Bush AI, Gamble JR, Shi B. Development of Novel Therapeutics Targeting the Blood-Brain Barrier: From Barrier to Carrier. Adv Sci (Weinh) 2021;:e2101090. [PMID: 34085418 DOI: 10.1002/advs.202101090] [Reference Citation Analysis]
41 Wong PK, Cheah FC, Syafruddin SE, Mohtar MA, Azmi N, Ng PY, Chua EW. CRISPR Gene-Editing Models Geared Toward Therapy for Hereditary and Developmental Neurological Disorders. Front Pediatr 2021;9:592571. [PMID: 33791256 DOI: 10.3389/fped.2021.592571] [Reference Citation Analysis]
42 Zou Y, Sun X, Wang Y, Yan C, Liu Y, Li J, Zhang D, Zheng M, Chung RS, Shi B. Single siRNA Nanocapsules for Effective siRNA Brain Delivery and Glioblastoma Treatment. Adv Mater 2020;32:2000416. [DOI: 10.1002/adma.202000416] [Cited by in Crossref: 26] [Cited by in F6Publishing: 15] [Article Influence: 26.0] [Reference Citation Analysis]
43 Berkowitz SA, Laue T. Boundary convection during velocity sedimentation in the Optima analytical ultracentrifuge. Anal Biochem 2021;:114306. [PMID: 34274312 DOI: 10.1016/j.ab.2021.114306] [Reference Citation Analysis]
44 Quinn J, Musa A, Kantor A, McClements ME, Cehajic-Kapetanovic J, MacLaren RE, Xue K. Genome-Editing Strategies for Treating Human Retinal Degenerations. Hum Gene Ther 2021;32:247-59. [PMID: 32993386 DOI: 10.1089/hum.2020.231] [Cited by in Crossref: 5] [Cited by in F6Publishing: 5] [Article Influence: 5.0] [Reference Citation Analysis]
45 Ulkoski D, Bak A, Wilson JT, Krishnamurthy VR. Recent advances in polymeric materials for the delivery of RNA therapeutics. Expert Opin Drug Deliv 2019;16:1149-67. [PMID: 31498013 DOI: 10.1080/17425247.2019.1663822] [Cited by in Crossref: 20] [Cited by in F6Publishing: 13] [Article Influence: 10.0] [Reference Citation Analysis]
46 Buck TM, Wijnholds J. Recombinant Adeno-Associated Viral Vectors (rAAV)-Vector Elements in Ocular Gene Therapy Clinical Trials and Transgene Expression and Bioactivity Assays. Int J Mol Sci 2020;21:E4197. [PMID: 32545533 DOI: 10.3390/ijms21124197] [Cited by in Crossref: 12] [Cited by in F6Publishing: 4] [Article Influence: 12.0] [Reference Citation Analysis]
47 Gorovits B, Marshall J, Smith J, Whiteley LO, Neubert H. Bioanalysis of adeno-associated virus gene therapy therapeutics: regulatory expectations. Bioanalysis 2019;11:2011-24. [DOI: 10.4155/bio-2019-0135] [Cited by in Crossref: 5] [Cited by in F6Publishing: 4] [Article Influence: 2.5] [Reference Citation Analysis]
48 Schlich M, Palomba R, Costabile G, Mizrahy S, Pannuzzo M, Peer D, Decuzzi P. Cytosolic delivery of nucleic acids: The case of ionizable lipid nanoparticles. Bioeng Transl Med 2021;:e10213. [PMID: 33786376 DOI: 10.1002/btm2.10213] [Cited by in Crossref: 5] [Cited by in F6Publishing: 4] [Article Influence: 5.0] [Reference Citation Analysis]
49 Viney L, Bürckstümmer T, Eddington C, Mietzsch M, Choudhry M, Henley T, Agbandje-McKenna M. Adeno-associated Virus (AAV) Capsid Chimeras with Enhanced Infectivity Reveal a Core Element in the AAV Genome Critical for both Cell Transduction and Capsid Assembly. J Virol 2021:JVI. [PMID: 33441336 DOI: 10.1128/JVI.02023-20] [Cited by in Crossref: 2] [Article Influence: 2.0] [Reference Citation Analysis]
50 Muhuri M, Zhan W, Maeda Y, Li J, Lotun A, Chen J, Sylvia K, Dasgupta I, Arjomandnejad M, Nixon T, Keeler AM, Manokaran S, He R, Su Q, Tai PWL, Gao G. Novel Combinatorial MicroRNA-Binding Sites in AAV Vectors Synergistically Diminish Antigen Presentation and Transgene Immunity for Efficient and Stable Transduction. Front Immunol 2021;12:674242. [PMID: 33995418 DOI: 10.3389/fimmu.2021.674242] [Reference Citation Analysis]
51 Tran NT, Heiner C, Weber K, Weiand M, Wilmot D, Xie J, Wang D, Brown A, Manokaran S, Su Q, Zapp ML, Gao G, Tai PWL. AAV-Genome Population Sequencing of Vectors Packaging CRISPR Components Reveals Design-Influenced Heterogeneity. Mol Ther Methods Clin Dev 2020;18:639-51. [PMID: 32775498 DOI: 10.1016/j.omtm.2020.07.007] [Cited by in Crossref: 8] [Cited by in F6Publishing: 4] [Article Influence: 8.0] [Reference Citation Analysis]
52 Jin Q, Qiao C, Li J, Li J, Xiao X. An engineered serum albumin-binding AAV9 capsid achieves improved liver transduction after intravenous delivery in mice. Gene Ther 2020;27:237-44. [DOI: 10.1038/s41434-019-0107-2] [Cited by in Crossref: 2] [Cited by in F6Publishing: 1] [Article Influence: 1.0] [Reference Citation Analysis]
53 Gong H, Yuan N, Shen Z, Tang C, Shipp S, Qian L, Lu Y, Andolina IM, Zhang S, Wu J, Yang H, Wang W. Transduction catalysis: Doxorubicin amplifies rAAV-mediated gene expression in the cortex of higher-order vertebrates. iScience 2021;24:102685. [PMID: 34195565 DOI: 10.1016/j.isci.2021.102685] [Reference Citation Analysis]
54 Tabrizi SJ, Flower MD, Ross CA, Wild EJ. Huntington disease: new insights into molecular pathogenesis and therapeutic opportunities. Nat Rev Neurol 2020;16:529-46. [PMID: 32796930 DOI: 10.1038/s41582-020-0389-4] [Cited by in Crossref: 26] [Cited by in F6Publishing: 17] [Article Influence: 26.0] [Reference Citation Analysis]
55 Chang YJ, Bae J, Zhao Y, Lee G, Han J, Lee YH, Koo OJ, Seo S, Choi YK, Yeom SC. In vivo multiplex gene targeting with Streptococcus pyogens and Campylobacter jejuni Cas9 for pancreatic cancer modeling in wild-type animal. J Vet Sci 2020;21:e26. [PMID: 32233134 DOI: 10.4142/jvs.2020.21.e26] [Cited by in Crossref: 3] [Cited by in F6Publishing: 2] [Article Influence: 3.0] [Reference Citation Analysis]
56 Adachi K, Dissen GA, Lomniczi A, Xie Q, Ojeda SR, Nakai H. Adeno-associated virus-binding antibodies detected in cats living in the Northeastern United States lack neutralizing activity. Sci Rep 2020;10:10073. [PMID: 32572045 DOI: 10.1038/s41598-020-66596-4] [Cited by in Crossref: 1] [Article Influence: 1.0] [Reference Citation Analysis]
57 Khorkova O, Hsiao J, Wahlestedt C. Nucleic Acid-Based Therapeutics in Orphan Neurological Disorders: Recent Developments. Front Mol Biosci 2021;8:643681. [PMID: 33996898 DOI: 10.3389/fmolb.2021.643681] [Reference Citation Analysis]
58 Chen X, He Y, Tian Y, Wang Y, Wu Z, Lan T, Wang H, Cheng K, Xie P. Different Serotypes of Adeno-Associated Virus Vector- and Lentivirus-Mediated Tropism in Choroid Plexus by Intracerebroventricular Delivery. Hum Gene Ther 2020;31:440-7. [PMID: 32056463 DOI: 10.1089/hum.2019.300] [Cited by in Crossref: 4] [Cited by in F6Publishing: 3] [Article Influence: 4.0] [Reference Citation Analysis]
59 Nguyen TNT, Sha S, Hong MS, Maloney AJ, Barone PW, Neufeld C, Wolfrum J, Springs SL, Sinskey AJ, Braatz RD. Mechanistic model for production of recombinant adeno-associated virus via triple transfection of HEK293 cells. Mol Ther Methods Clin Dev 2021;21:642-55. [PMID: 34095346 DOI: 10.1016/j.omtm.2021.04.006] [Cited by in Crossref: 1] [Cited by in F6Publishing: 1] [Article Influence: 1.0] [Reference Citation Analysis]
60 Clarner P, Lau SK, Chowdhury T, Guilmette E, Trapa P, Lo S, Shen S. Development of a one-step RT-ddPCR method to determine the expression and potency of AAV vectors. Molecular Therapy - Methods & Clinical Development 2021;23:68-77. [DOI: 10.1016/j.omtm.2021.05.003] [Cited by in Crossref: 1] [Cited by in F6Publishing: 1] [Article Influence: 1.0] [Reference Citation Analysis]
61 Zhou H, Zhang S, Lv F, Sun W, Wang L, Fan C, Li J, Hu J. Citrate-assisted efficient local delivery of naked oligonucleotide into live mouse brain cells. Cell Prolif 2019;52:e12622. [PMID: 31062905 DOI: 10.1111/cpr.12622] [Cited by in Crossref: 1] [Cited by in F6Publishing: 2] [Article Influence: 0.5] [Reference Citation Analysis]
62 Bode D, Cull AH, Rubio-Lara JA, Kent DG. Exploiting Single-Cell Tools in Gene and Cell Therapy. Front Immunol 2021;12:702636. [PMID: 34322133 DOI: 10.3389/fimmu.2021.702636] [Reference Citation Analysis]
63 Privolizzi R, Chu WS, Tijani M, Ng J. Viral gene therapy for paediatric neurological diseases: progress to clinical reality. Dev Med Child Neurol 2021;63:1019-29. [PMID: 33834479 DOI: 10.1111/dmcn.14885] [Reference Citation Analysis]
64 Oh TJ, Fan H, Skeeters SS, Zhang K. Steering Molecular Activity with Optogenetics: Recent Advances and Perspectives. Adv Biol (Weinh) 2021;5:e2000180. [PMID: 34028216 DOI: 10.1002/adbi.202000180] [Cited by in Crossref: 2] [Cited by in F6Publishing: 2] [Article Influence: 2.0] [Reference Citation Analysis]
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